Q. 13 The first clinical gene therapy was done for the treatment of
(c) Cystic fibrosis
(d) SCID (Severe Combined Immuno Deficiency) resulting from the deficiency of ADA
The SCID patient has a defective gene for the enzyme Adenosine Deaminase (ADA) due to which he/she lacks functional T-lymphocytes and therefore, fails to fight the infecting pathogen.